Determining minimal clinically important differences in the North Star Ambulatory Assessment (NSAA) for patients with Duchenne muscular dystrophy.

Gupta V, Ayyar; JM, Pitchforth; J, Domingos; D, Ridout; M, Iodice; C, Rye; M, Chesshyre; A, Wolfe; V, Selby; A, Mayhew; ES, Mazzone; V, Ricotti; JY, Hogrel; EH, Niks; Groot I, de; L, Servais; V, Straub; E, Mercuri; AY, Manzur; F, Muntoni

doi:10.1371/journal.pone.0283669

Public

Determining minimal clinically important differences in the North Star Ambulatory Assessment (NSAA) for patients with Duchenne muscular dystrophy.

Shared by NobleBlocks on Apr 26, 2023 • 12:00 AM UTC

Authors:

Ayyar Gupta V

Pitchforth JM

Domingos J

Abstract

The North Star ambulatory assessment (NSAA) is a functional motor outcome measure in Duchenne muscular dystrophy (DMD), widely used in clinical trials and natural history studies, as well as in clinical practice. However, little has been reported on the minimal clinically important difference (MCID)...

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