Determining minimal clinically important differences in the North Star Ambulatory Assessment (NSAA) for patients with Duchenne muscular dystrophy

Ayyar Gupta, V.; Pitchforth, J.; Domingos, J.; Ridout, D.; Iodice, Mario; Rye, C.; Chesshyre, M.; Wolfe, Amy; Selby, V.; Mayhew, A.; Mazzone, E.; Ricotti, V.; Hogrel, J.; Niks, E.; J. M. de Groot, Imelda; Servais, L.; Straub, V.; Mercuri, Eugenio; Manzur, A.; Muntoni, F.

doi:10.1371/journal.pone.0283669

Public

Determining minimal clinically important differences in the North Star Ambulatory Assessment (NSAA) for patients with Duchenne muscular dystrophy

Shared by NobleBlocks on Apr 26, 2023 • 12:00 AM UTC

Authors:

V. Ayyar Gupta

J. Pitchforth

J. Domingos

Abstract

The North Star ambulatory assessment (NSAA) is a functional motor outcome measure in Duchenne muscular dystrophy (DMD), widely used in clinical trials and natural history studies, as well as in clinical practice. However, little has been reported on the minimal clinically important difference (MCID)...

Subject

Medicine

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